New FDA-approved gene therapy for kids will cost record $4.25 million
A new one-time gene therapy that treats a rare disease in children will cost an eye-popping $4.25 million, making it the world’s most expensive drug. The Food and Drug Administration approved Lenmeldy, the first drug able to treat metachromatic leukodystrophy, on Monday. The gene therapy will treat the condition in infants and children both before […]